Jean Mah

Dr. Jean Mah

Principal Applicant

Pediatrics and Clinical Neurosciences Professor at the Cumming School of Medicine

Pediatric Neurologist and the Director of the Pediatric Neuromuscular Program at the Alberta Children’s Hospital


NMD4C Involvement: Pillar 2: Clinical Research, Theme 5: Open Science

Biography

Dr. Jean Mah is a pediatric neurologist and the director of the Pediatric Neuromuscular Program at the Alberta Children’s Hospital in Calgary, Alberta, Canada. She is a Professor of Pediatrics and Clinical Neurosciences at the Cumming School of Medicine, University of Calgary.  She is currently involved in multicenter clinical research studies related to pediatric neuromuscular diseases.  


Recent Publications

Degan, C, Tobin, RA, de Vries, SI, Jiménez-Requena, A, Peco, A, Guglieri, M et al.. Evaluation of a serum protein signature as monitoring biomarker for Duchenne muscular dystrophy in a long-term clinical trial with corticosteroids. Skelet Muscle. 2026. PMID:42443978

Mah, JK, Lochmüller, H, Ward, L, Selby, K, Gonorazky, H, Sbrocchi, AM et al.. Expanding Vamorolone Treatment Access for Canadians with Duchenne Muscular Dystrophy. Can J Neurol Sci. 2026. 1-4 PMID:42438401

Schellenberg, KL, Osman, H, Masnata, M, Hicks, R, Kagan, C, Stosic, A et al.. Implementation of a neuromuscular clinical trial network: a rare disease model for enhancing clinical trial readiness, capacity, and access in Canada. Orphanet J Rare Dis. 2026.21 (1) PMID:42192450

Mah, JK, Gonorazky, HD, Nigro, E, Lochmüller, H, Alemán, A, Yaworski, A et al.. Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys. Neurology. 2026.106 (11)e218066 PMID:42139656

Lochmüller, H, Gonorazky, H, Nigro, E, Mah, JK, Alemán, A, Yaworski, A et al.. Results of a phase II open-label, multiple-dose study of vamorolone (VBP15-006) in 7- to < 18-year-old boys with duchenne muscular dystrophy. J Neurol. 2026.273 (3) PMID:41774261

Mummidivarpu, S, Dang, UJ, Ziemba, M, Hathout, Y, Clemens, PR, Damsker, J et al.. Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4- to <7-year children. Steroids. 2026.225 109721 PMID:41265551

Ahmadiharchegani, F, Tobin, RA, Degan, C, Naveed, A, Guglieri, M, Jiménez-Requena, A et al.. Circulating protein biomarkers identified in two independent clinical trial cohorts of glucocorticoid-naive Duchenne muscular dystrophy patients. Sci Rep. 2025.15 (1)39997 PMID:41238663

Dussah, N, McKim, DA, Mah, JK, McMillan, HJ, Campbell, C, Bijelić, V et al.. Patterns of Adherence to Lung Volume Recruitment Therapy Amongst Individuals With Duchenne Muscular Dystrophy: A Secondary Analysis of the STEADFAST Randomized Controlled Trial. Pediatr Pulmonol. 2025.60 (10)e71357 PMID:41147267

Price, TR, Mah, JK. Reviewer Comment on Slayter et al. "An Exploratory 12-Month Observational Study of Adults with Spinal Muscular Atrophy: Learning from Our Tools". Can J Neurol Sci. 2025. 1 PMID:41039820

Iraqi, I, Ng, P, Chen, X, Cushen, N, Gottowik, J, Herzig, D et al.. Feasibility of a Home-Based Exergaming Intervention for Youth With Spinal Muscular Atrophy. Muscle Nerve. 2025.72 (6)1259-1264 PMID:40990108

See more on PubMed