SMA Outcome Measures Training for Physiotherapists and Occupational Therapists
As a part of the NMD4C’s clinical research work pillar, we are supporting the development and training on validated NMD outcome measures. Considering the evolving therapeutic landscape of Spinal muscular atrophy (SMA) and the need for high-quality real-world data, convening clinicians to discuss and train on nationally agreed-upon outcome measures (OM) will enhance our capacity to uncover significant disease trajectory patterns and therapy responses.
In March, we provided an opportunity for physiotherapists and occupational therapists to attend our first training session of this kind for outcome measures in SMA.
To complement this training session, we will host an English-language training on standardizing assessment practices in SMA outcome measures later in 2024, which will include the learnings from the March training session in Quebec. We will reach out to share more information on this English-language training session when details are available.
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Could You Be Our Next Awardee? Meet Jules Granet, NMD4C’s 2026 Publication of the Year Awardee
Nominations are open till by 18 January 2027!
In 2026, Jules Granet, a PhD Candidate at McGill University and trainee in Dr. Natasha Chang’s laboratory received an NMD4C Publication of the Year Award for research investigating how muscle stem cell dysfunction contributes to impaired muscle regeneration in Duchenne muscular dystrophy. Nominate yourself or a neuromuscular colleague whose research, clinical care, leadership, advocacy, or community contributions deserve to be recognized.
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