Video Abstracts
Published recently in Annals of Neurology, this video abstract is of a study by Dr. Emma Sutton titled “Maternal-Fetal Administration of Risdiplam Partially Rescues the SMNΔ7 Mouse Model of Spinal Muscular Atrophy(opens in new tab)” which explores the potential of early prenatal therapeutic interventions for Spinal Muscular Atrophy (SMA).
This video abstract presents Jules Granet’s work from Dr. Natasha Chang’s lab titled “Muscle stem cells in Duchenne muscular dystrophy exhibit molecular impairments and altered cell fate trajectories impacting regenerative capacity”, published recently in Cell Death & Disease. This investigates how muscle stem cell dysfunction contributes to impaired muscle regeneration in Duchenne muscular dystrophy and how targeting autophagy could help to improve their regenerative capacity.