The Neuromuscular Disease Network for Canada (NMD4C) and Muscular Dystrophy Canada (MDC) are pleased to invite you to a webinar on clinical updates on Modelling SMA: Progress and Future Prospects.

This webinar is primarily targeted at Canadian clinicians, academics, and trainees with an interest in neuromuscular disease. NMD4C and MDC are providing organizational and technical support. There is no involvement and influence from industry.

Register Now!

Chair:

• Dr. Kessen Patten

Speakers:

• Dr. Alex Parker: Genetic models of neuromuscular disease
• Dr. Rashmi Kothary: Peripheral organ gene therapy is important in SMA
• Dr. Stefano Stifani: Harnessing the potential of IPSC-derived neurons and glia for modelling SMA and other motor neuron diseases

Learning objectives:

1. What are the routes of administration of AAV vectors for gene therapy in SMA?
2. Is restoring SMN to sites other than the central nervous system important for treatment in SMA?
3. How to model neuromuscular disorders in the invertebrate C. elegans.
4. Collaborative translational approaches using C. elegans.
5. How to take cellular heterogeneity into consideration when modeling motor neuron disease using human iPSCs.

The NMD Rounds & Educational Webinars is a self-approved group learning activity (Section 1) as defined by the Maintenance of Certification Program of the Royal College of Physicians and Surgeons of Canada.