NMD4C: The Neuromuscular Disease Network for Canada

As a part of the NMD4C’s clinical research work pillar, we are supporting the development and training on validated NMD outcome measures. Considering the evolving therapeutic landscape of Spinal muscular atrophy (SMA) and the need for high-quality real-world data, convening clinicians to discuss and train on nationally agreed-upon outcome measures (OM) will enhance our capacity to uncover significant disease trajectory patterns and therapy responses. 

In March, we provided an opportunity for physiotherapists and occupational therapists to attend our first training session of this kind for outcome measures in SMA.

To complement this training session, we will host an English-language training on standardizing assessment practices in SMA outcome measures later in 2024, which will include the learnings from the March training session in Quebec. We will reach out to share more information on this English-language training session when details are available.