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News Release: Neuromuscular Disease Registry Helps Patients Access Research, Clinical Trials, New Genetic Tests, and Therapies

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2020 NMD4C Year in Review

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Dr. Bernard Brais Featured in The Economist Report on Navigating Rare Neurological Diseases

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Latest edition of the Journal of Neuromuscular Diseases now online – Sep 2020

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Letter to provincial governments regarding SMA therapy outcome measures

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A national spinal muscular atrophy registry for real world evidence

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Upcoming webinar: The genetics of congenital myopathies in French Canadians

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Exciting research grants awarded by Jesse’s Journey